A new study from the University of Ottawa’s Faculty of Medicine sheds light on a potential breakthrough in treating muscle ...
Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...
A two-and-a-half-year-old girl shows no signs of a rare genetic disorder, after becoming the first person to be treated for ...