A pioneering team at St Jude Children's Research Hospital in the US say they successfully treated a child diagnosed with SMA ...
Roche dévoile une technologie exclusive et révolutionnaire de séquençage par expansion , qui 'offre un séquençage ...
Le gel de l'aide étrangère par le gouvernement américain a bouleversé la chaîne d'approvisionnement en produits médicaux ...
a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), announced today that the U.S. Food and Drug Administration (FDA) has approved a New Drug Application (NDA) for an Evrysdi® (risdiplam ...
Ionis relies on upfront payments and licensing fees from partners, as well as Spinraza royalties, to drive revenue today, but its rapidly advancing portfolio should help diversify revenue. 2025 is ...
Basel: Roche, announced that the U.S. Food and Drug Administration (FDA) has approved a New Drug Application (NDA) for an ...
The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results, a case report indicated. More than 2 ...
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
It has emerged from the same drug discovery engine that generated Roche's spinal muscular atrophy (SMA) therapy Evrysdi (risdiplam), which made $1.5 billion in sales last year. PTC recently ...